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PDFOct 02, 2019 | Spinal Muscular Atrophy WMS 2019 Spinal Muscular Atrophy
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PDFOct 02, 2019 | Spinal Muscular Atrophy WMS 2019 Spinal Muscular Atrophy
RAINBOWFISH: A study of risdiplam (RG7916) in newborns with pre-symptomatic spinal muscular atrophy (SMA)
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PDFOct 02, 2019 | Spinal Muscular Atrophy WMS 2019 Spinal Muscular Atrophy
JEWELFISH: Safety and pharmacodynamic data in patients with spinal muscular atrophy (SMA) receiving treatment with risdiplam (RG7916) that have previously been treated with nusinersen