ICNMD 2024

Oct 25 - Oct 29, 2024 | Perth, Australia

Share this page

Close Tooltip
Copy Link Tooltip

Copy page URL

Watch webcast footage from the symposium: Preparing for a future with gene therapy in DMD: A journey towards inclusion and equity

Authors Ian Woodcock, Francesco Muntoni, Michelle Lorentzos

Published date12 November, 2024

The DMD Symposium at ICNMD: Explored the practical and ethical challenges around introducing gene therapy as a potential treatment option for DMD. Examined the available clinical data for DMD gene therapies in the context of disease progression, outcome measures and safety signals. Highlighted important considerations to overcome identified challenges associated with gene therapy delivery.

Welcome to Medically

The Roche Science Hub

This website is a non-promotional global resource intended to facilitate transparent scientific exchange regarding developments in medical research, diagnostics, and disease management.

Not a healthcare professional? Browse:

This website is a non-promotional global resource intended to facilitate transparent scientific exchange regarding developments in medical research, diagnostics, and disease management. This global website is intended for healthcare professionals outside the UK, US, Canada, and Australia. The content on this website may include scientific information about experimental or investigational compounds, indications, and services that are not approved or valid in your country. Registration status and prescribing information of medicinal products may differ between countries. Please refer to local product information for any medicinal products mentioned on this website. Information available on this website does not constitute professional medical advice, and Roche and Genentech accept no responsibility for access to or use of the same.

You are Leaving Medically

By following this link, you are leaving Roche Website and entering a site that is not owned or controlled by Roche. Roche does not take any responsibility for acces to or use of this website, nor for any content therein.

You are Leaving the Global Medically Site

By following this link, you are being redirected to another Roche page.